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261,768 grants matching “gene therapy”
Organ specific microenvironmental regulation of metastasis
$871,771Kandice Tanner · Division Of Basic Sciences - Nci · ZIA · FY2025 · CA
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2019 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2017 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2023 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2021 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2018 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2022 · NS
Pathogenesis of Neurological Disability in Primary Diseases of Myelin
$871,750Bruce D Trapp · Cleveland Clinic Lerner Com-Cwru · R35 · FY2020 · NS
DNA Repair and Genomic Instability in Cancer Development and Therapy
$871,725Jean Gautier · Columbia University Health Sciences · R35 · FY2019 · CA
A Pharmacochaperone-based strategy for identifying chemical probes of brain-derived orphan GPCRs
$871,671Michael Jackson · Sanford Burnham Prebys Medical Discovery Institute · R01 · FY2023 · MH
EPIDEMIOLOGY AND GENETICS OF PARKINSON'S DISEASE
$871,620Mayo Clinic Coll Of Medicine, Rochester · R01 · FY2003 · NS
Discovery of Molecules to disrupt the outer membrane of Gram-negative pathogens
$871,618Daniel E Kahne · Harvard Medical School · U19 · FY2014 · AI
MOLECULAR THERAPY FOR CF AND GENETIC DISEASES
$871,527James M Wilson · University Of Pennsylvania · P30 · FY2006 · DK
Identifying driver mutations and tumor dependencies by comparative oncogenomics.
$871,519Scott W Lowe · Cold Spring Harbor Laboratory · U01 · FY2010 · CA
LncRNA mechanisms in cancer
$871,453Howard Y Chang · Stanford University · R35 · FY2021 · CA
Leber Hereditary Optic Neuropathy: Gene Therapy Trial
$871,453John R Guy · University Of Miami School Of Medicine · R24 · FY2008 · EY
Regulation of diverse microglial phenotypes in neurodegeneration
$871,419Suman Jayadev · University Of Washington · R56 · FY2023 · AG
Chronic Renal Insufficiency and Silent Progression of Aortic Stenosis (CRISP-AS)
$871,361Jordan Blair Strom · Beth Israel Deaconess Medical Center · R01 · FY2023 · HL
Ca2+ signaling Networks in Health and Disease
$871,274Mohamed Trebak · University Of Pittsburgh At Pittsburgh · R35 · FY2024 · HL
Immune selection of HIV-1 reservoir cells in human clinical trials
$871,246Mathias Lichterfeld · Brigham And Women'S Hospital · R01 · FY2025 · AI
Mechanisms of Cell-Based Heart Regeneration
$871,202Charles E Murry · University Of Washington · R01 · FY2021 · HL
Mechanisms of Cell-Based Heart Regeneration
$871,202Nathan John Sniadecki · University Of Washington · R01 · FY2022 · HL
Mechanisms of Cell-Based Heart Regeneration
$871,202Charles E Murry · University Of Washington · R01 · FY2020 · HL
Regulation of Differentiation of Pediatric Embryonal Tumors- Neuroblastoma
$871,159Carol Thiele-Galetto · Division Of Basic Sciences - Nci · ZIA · FY2016 · CA
Modeling drugs of abuse-HIV interactions using iPSC-derived human cerebral organoids
$871,147Pietro P Sanna · Scripps Research Institute, The · R01 · FY2022 · DA