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261,768 grants matching “gene therapy”
Cellular Regulation in Genitourinary Development
$901,268University Of Virginia Charlottesville · P50 · FY2003 · DK
Cellular Regulation in Genitourinary Development
$901,268University Of Virginia Charlottesville · P50 · FY2005 · DK
Effect of tumor editing on antitumor immunity
$901,205Judy Lieberman · Boston Children'S Hospital · R35 · FY2025 · CA
Retinal Circuit Development & Genetics
$900,981Tudor Badea · National Eye Institute · ZIA · FY2012 · EY
DNA Repair and Genomic Instability in Cancer Development and Therapy
$900,969Jean Gautier · Columbia University Health Sciences · R35 · FY2017 · CA
Cellularly resolved molecular pathway assessment in biopsies via spectral imaging
$900,963Richard M. Levenson · Cambridge Research And Instrumentation · R44 · FY2009 · CA
Gene Therapy for Batten Disease Using AAVrh.10 Expressing Human CLN2 cDNA
$900,949Ronald G Crystal · Weill Medical Coll Of Cornell Univ · R01 · FY2010 · NS
Development Of Theoretical Methods For Studying Biological Macromolecules
$900,908Bernard R Brooks · National Heart, Lung, And Blood Institute · ZIA · FY2015 · HL
Preclinical Testing of Drug Combinations (HDAC, mTOR, CDK and MYC Inhibitors)
$900,771Beverly Mock · Division Of Basic Sciences - Nci · ZIA · FY2020 · CA
Targeting regulators of cellular gene transcription to impact HIV latency
$900,756Douglas D Richman · Veterans Medical Research Fdn/San Diego · P01 · FY2009 · AI
Modeling KRAS-Dependent Synthetic Lethality in Human Colon Organoids
$900,713Calvin J Kuo · Stanford University · U01 · FY2019 · CA
Epigenetics, Stem Cells, and Cancer
$900,709Rudolf Jaenisch · Whitehead Institute For Biomedical Res · R01 · FY2010 · CA
Drug Resistance Genotypic and Phenotypic Correlates of Efavirenz and Dolutegravir based Treatment Outcomes across Non-B HIV-1 subtypes
$900,704Lisa M Frenkel · Seattle Children'S Hospital · R01 · FY2019 · AI
Preventing Anthracycline Cardiovascular Toxicity with Statins
$900,665William Gregory Hundley · Wake Forest University Health Sciences · R01 · FY2016 · HL
Anti-Fibrotic Therapy for Pulmonary Fibrosis
$900,595Latha Paka · Angion Biomedica Corporation · R44 · FY2007 · HL
Prospective studies on Parkinson's disease
$900,537Honglei Chen · National Institute Of Environmental Health Sciences · ZIA · FY2009 · ES
S.japonicum and pregnancy outcomes: an RCT
$900,505Jennifer F Friedman · Rhode Island Hospital · U01 · FY2010 · AI
Human Variants
$900,503Joann B Sweasy · University Of Vermont & St Agric College · P01 · FY2012 · CA
Whole-genome sequencing in multiplex epilepsy families
$900,501David B. Goldstein · Duke University · RC2 · FY2010 · NS
(Epi)genetic Risk Architectures in Opioid Dependent Brain
$900,490Peter Christopher Scacheri · Case Western Reserve University · R01 · FY2019 · DA
Epigenetic damage in women living in LA food-desert zip codes
$900,360Victoria L. Seewaldt · Beckman Research Institute/City Of Hope · R01 · FY2020 · CA
Multicellular Mechanisms Driving Axon Regeneration
$900,228Valeria Cavalli · Washington University · R35 · FY2023 · NS
Role of Trk Receptors in the Development and Function of Non-neuronal Structures
$900,224Lino Tessarollo · Division Of Basic Sciences - Nci · ZIA · FY2025 · CA
Role of Neurotrophins in the Development of the Mammalian Nervous System
$900,224Lino Tessarollo · Division Of Basic Sciences - Nci · ZIA · FY2025 · CA
Proteomics Core
$900,205S Munir Alam · Duke University · U19 · FY2010 · AI