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261,768 grants matching gene therapy

Lysosomal NADPH metabolism regulates proteostasis, aging and tauopathy

$1,591,453
Weiwei Dang · Baylor College Of Medicine · RF1 · FY2021 · AG

ADP-ribosylation Cycles

$1,591,105
Joel Moss · National Heart, Lung, And Blood Institute · ZIA · FY2024 · HL

Molecular Targets for Drug and Radiation Sensitivity

$1,591,052
Stephen M Hahn · University Of Pennsylvania · P01 · FY2006 · CA

Mental Retardation &Developmental Disabilities Research

$1,590,796
Children'S Hospital Boston · P30 · FY2003 · HD

Telomeres Diseases

$1,590,725
Neal S Young · National Heart, Lung, And Blood Institute · ZIA · FY2011 · HL

Multiscale Analysis of Immune Responses

$1,590,437
Ronald Germain · National Institute Of Allergy And Infectious Diseases · ZIA · FY2022 · AI

A Program for Innovative PET Radioligand Development and Application - A Translational Toolbox for Treatments for Mental Health

$1,590,284
Richard E Carson · Yale University · U01 · FY2024 · MH

A Program for Innovative PET Radioligand Development and Application - A Translational Toolbox for Treatments for Mental Health

$1,590,284
Richard E Carson · Yale University · U01 · FY2025 · MH

A Program for Innovative PET Radioligand Development and Application - A Translational Toolbox for Treatments for Mental Health

$1,590,284
Richard E Carson · Yale University · U01 · FY2023 · MH

Clonal analysis of in vivo hematopoiesis

$1,590,278
Cynthia E Dunbar · National Heart, Lung, And Blood Institute · ZIA · FY2017 · HL

NHGRI/DIR Technology Transfer Program

$1,590,131
Daniel Kastner · National Human Genome Research Institute · ZIK · FY2011 · HG

A Phase I Clinical Trial Testing Feasibility of Hematopoietic Stem Cell Gene Therapy Using Platelet Factor VIII to Safely Improve Hemostasis for Severe Hemophilia A with Inhibitory Antibodies

$1,589,707
David Allen Wilcox · Medical College Of Wisconsin · R01 · FY2022 · HL

Center for the Neurobiology of Addiction Treatment

$1,589,690
Michael A Nader · Wake Forest University Health Sciences · P50 · FY2019 · DA

SPORE in Ovarian Cancer

$1,589,106
Ie-Ming Shih · Johns Hopkins University · P50 · FY2022 · CA

Rare Disease Network for Myasthenia Gravis

$1,588,974
Henry J Kaminski · George Washington University · U54 · FY2022 · NS

Understanding and Improving Therapies for the Muscular Dystrophies

$1,588,673
Hugh Lee Sweeney · University Of Florida · P50 · FY2021 · AR

Marinobufagenin as a therapeutic target

$1,588,518
Edward Lakatta · National Institute On Aging · ZIA · FY2020 · AG

HIV Persistence During Suppressive Antiretroviral Therapy

$1,588,506
Frank Maldarelli · Division Of Basic Sciences - Nci · ZIA · FY2024 · CA

Parkinson's Disease Gene Therapy Study Group

$1,588,339
University Of Rochester · U54 · FY2005 · NS

Development and Preclinical Applications of Pancreatic Adenocarcinoma Models

$1,588,248
Shyam Sharan · Division Of Basic Sciences - Nci · ZIA · FY2018 · CA

Mechanisms Of Action Of Psychoactive Drugs

$1,588,148
De-Maw Chuang · National Institute Of Mental Health · ZIA · FY2014 · MH

Development of Recombinant Toxins to Treat Hematologic Malignancies

$1,588,137
Robert Kreitman · Division Of Basic Sciences - Nci · ZIA · FY2024 · CA

Development of PU.1 Inhibitory Modulators as Novel Therapeutics for Alzheimer's Disease

$1,587,671
Li-Huei Tsai · Massachusetts Institute Of Technology · U01 · FY2022 · AG

Expression Genetics in Drug Therapy

$1,587,669
Wolfgang Sadee · Ohio State University · U01 · FY2014 · GM

Prostate Cancer Bone Metastasis Biology and Targeting

$1,587,650
Michael R Freeman · Cedars-Sinai Medical Center · P01 · FY2019 · CA