← SearchGENE THERAPY FOR LYSOSOMAL STORAGE DISEASE$306,400R01FY2000NSNIHResearch Inst Nationwide Children'S Hosp, Columbus OHInvestigatorsThomas SferraLinked publications & trialsPaper 18245552Paper 17317838Paper 16778107Paper 15336648Paper 12900769View original record on NIH RePORTER →