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ALLELE-SPECIFIC PROTEIN-BASED THERAPEUTICS FOR AMYOTROPHIC LATERAL SCLEROSIS ASSOCIATED WITH C9ORF72 REPEAT EXPANSIONS

$496,427FY2022Defense Health AgencyDOD

Enzerna Biosciences Llc

Investigators

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ALLELE-SPECIFIC PROTEIN-BASED THERAPEUTICS FOR AMYOTROPHIC LATERAL SCLEROSIS ASSOCIATED WITH C9ORF72 REPEAT EXPANSIONS · GrantIndex