← SearchGene Therapy Platform for Rare Diseases$5,164,330ZIAFY2020TRNIHNational Center For Advancing Translational SciencesInvestigatorsDonald LocontactLinked publications, trials & patentsPaper 36694456Paper 32775499Paper 32593511Paper 31327755Paper 30706404Paper 30648435Paper 30518686Paper 29902280Paper 28793798Paper 28398005Paper 27378693Paper 26784641View original record on NIH RePORTER →